ProQR Therapeutics NV has announced a significant milestone in their ongoing development of RNA therapies. The company has submitted a Clinical Trial Application $(CTA.UK)$ for their product AX-0810, which targets NTCP for the treatment of cholestatic diseases. This submission marks a key step forward for ProQR as they continue to advance their proprietary Axiomer™ RNA editing technology platform. The news comes ahead of ProQR's upcoming presentation at the RNA Editing Summit in Boston, where further details on their CNS applications and Rett program will be discussed.
Disclaimer: This news brief was created by Public Technologies (PUBT) using generative artificial intelligence. While PUBT strives to provide accurate and timely information, this AI-generated content is for informational purposes only and should not be interpreted as financial, investment, or legal advice. ProQR Therapeutics NV published the original content used to generate this news brief via GlobeNewswire (Ref. ID: GNW1001119801-en) on July 28, 2025, and is solely responsible for the information contained therein.
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