Opus Genetics Advances BEST1 Gene Therapy Trial After Positive Safety Review

Reuters12-09

<a href="https://laohu8.com/S/IRD">Opus Genetics</a> Advances BEST1 Gene Therapy Trial After Positive Safety Review

Opus Genetics Inc. has announced a positive recommendation from the Independent Data Monitoring Committee (IDMC) to continue its Phase 1/2 clinical trial evaluating OPGx-BEST1, a gene therapy for Best disease. The recommendation follows a pre-specified safety review of one-month data from the sentinel participant, which demonstrated an initial favorable safety profile. Based on these results, the company will proceed with dosing the next four participants in the trial. No efficacy results have been presented at this stage.

Disclaimer: This news brief was created by Public Technologies (PUBT) using generative artificial intelligence. While PUBT strives to provide accurate and timely information, this AI-generated content is for informational purposes only and should not be interpreted as financial, investment, or legal advice. Opus Genetics Inc. published the original content used to generate this news brief via GlobeNewswire (Ref. ID: GNW9598776-en) on December 09, 2025, and is solely responsible for the information contained therein.

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