- Beam Therapeutics reported interim Phase 1/2 BEACON trial results for investigational sickle cell therapy risto-cel in New England Journal of Medicine.
- Data were initially presented at American Society of Hematology annual meeting, then updated in journal publication.
- Study showed patients had sustained improvement in disease biology with elimination of severe pain crises following engraftment.
- Beam expects U.S. BLA submission for risto-cel as early as year-end 2026.
- Company pegged eligible U.S. sickle cell population for gene therapies at about 10,000 patients.
Disclaimer: This news brief was created by Public Technologies (PUBT) using generative artificial intelligence. While PUBT strives to provide accurate and timely information, this AI-generated content is for informational purposes only and should not be interpreted as financial, investment, or legal advice. Beam Therapeutics Inc. published the original content used to generate this news brief via GlobeNewswire (Ref. ID: 202604011712PRIMZONEFULLFEED9683015) on April 01, 2026, and is solely responsible for the information contained therein.
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